Gene Therapy for SMA: An Emerging Treatment Option for a Devastating Disease
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Gene Therapy for SMA: An Emerging Treatment Option for a Devastating Disease
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Activity Info
Supplement in The Journal of Managed Care & Specialty Pharmacy discusses current knowledge about SMA, provides clinical evidence for available and emerging treatment options, and presents approaches for adding new therapies to hospital/health system formularies to ensure timely access to newly approved therapies for SMA.