As new therapies emerge for Duchenne's Muscular Dystrophy and Limb Girdle Muscular Dystrophy that include gene therapy and RNA exon-skipping therapies, clinicians need to consider the expectations for these treatments. Experts, Dr. Eugenio Mercuri, Dr. Jerry Mendell and Dr. Brenda Wong, recently discussed these emerging therapies and their implications on the clinical disease state following an international meeting.